Orphan Drug Act 30th Anniversary

It's been three decades since

... the

Rare Disease Day: A Look at 40 Years of the

It's been three decades since

Video abstract of review paper "A

... Alexion, AstraZeneca Rare Disease) Rare Disease Day: A Look at 40 Years of the

... Foundation as she talked about the advances made in the rare disease community since the passing of the

The authors of RAPS'

... awards to heroes of the rare disease community at the

Watch the presentation to hear us discuss the importance of the

Paul Melmeyer, Director of Federal Policy, National Organization for Rare Disorders Cartier Esham, Executive Vice President for ...

Health Canada plans to introduce its

... awards to heroes of the rare disease community at the

Last week, we argued that the benefits of the

Emil Kakkis, MD, President and Founder of Ultragenyx Pharmaceutical Inc., explains that while the

Drug companies love the

Welcoming Remarks and Panel 1 (Contextual Considerations and Ethical Issues)

Are you developing medicines for rare diseases? If so, our new video from a recent webinar can give you advice on how to devise ...

Rare Disease Legislation: A Historical Primer |

Panel 4 (Price, Cost-Effectiveness, and Affordability) and Adjournment Please note the following correction at 32:15: Patrick ...